• closedAccess   Exon skipping in Duchenne muscular dystrophy 

      Martorell Ménsua, Laura Merçé Universitat Jaume I (2020-04-28)
      Duchenne muscular dystrophy (DMD) is the most common form of muscular dystrophy. Current treatment for this disease focuses on a symptomatic approach, however, mutation-specific therapies have gained regulatory approval, ...